Ownership
Public
Employees
~2100
Therapeutic Areas
Rare DiseasesCardiovascular
Stage
Commercial
Preclinical
Phase 1
Phase 2
Phase 3
Approved
Modalities
RNA interference (RNAi)Small interfering RNA (siRNA)

Alnylam Pharmaceuticals General Information

Alnylam is the global leader in RNA interference therapeutics with five approved medicines as of 2025. Its drugs have demonstrated significant efficacy for rare genetic diseases such as hATTR amyloidosis, acute hepatic porphyria, primary hyperoxaluria type 1, and cardiovascular disease. The company continues to expand its clinical pipeline into new indications and organ systems beyond the liver

Contact Information

Primary Industry
Biotech
Corporate Office
Cambridge, Massachusetts
United States

Drug Pipeline

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Commercial
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Drug Asset 2
Phase X
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Drug Asset 3
Phase X
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Key Partnerships

Novartis (Leqvio), Regulus Therapeutics (co-founded with Ionis), past partnerships with Medtronic, Biogen Idec/Biogen Inc., Hoffmann-La Roche/Ionis Pharmaceuticals

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Alnylam Pharmaceuticals Funding

No funding data available

Early Stage VC (Series A)04-Jun-2020$38MCompletedPhase 1
Seed Round12-Feb-2019$8.5MCompletedStartup

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Alnylam Pharmaceuticals Financial Metrics

Market Cap
$41920.8M
Total Revenue
$1097.0M
Enterprise Value
$40290.7M