Company intelligence / Profile preview
Rocket Pharmaceuticals, Inc.
Cranbury, New Jersey, United Statesrocketpharma.com ↗
- Ownership
- Public · RCKT
- Employees
- ~150
- Development stage
- Phase 2
01
Overview
Advancing multiple gene therapy programs with positive Phase 1 results for RP-A501 for Danon Disease; initiated rolling BLA for RP-L102 for Fanconi Anemia; FDA review ongoing for KRESLADI for LAD-I; Phase 1 trial of RP-A601 for PKP2-ACM ongoing with data expected in first half of 2025
- Therapeutic areas
- HematologyImmunologyRare DiseasesCardiovascular
- Modalities
- Gene therapy (ex vivo lentiviral vector and in vivo adeno-associated viral vector)
- Industry
- Biotech
02
Drug pipeline
17 assets16 more assets in the full pipeline.
Request access →03
Partnerships
Children's Hospital of Philadelphia (CHOP)Temple UniversityREGENXBIOMemorial Sloan Kettering Cancer CenterNYUCIRMUniversity of MinnesotaStanford Medical SchoolForty Seven (a Gilead company)University of ColoradoUCLAUCSDFred Hutchinson Cancer Research CenterCIBERCIBERERCIEMATUniversity College London Great Ormond Street Hospital for ChildrenLund UniversityMolMedUniversity of Hannover
04
Financials
- Market cap
- $396.4M
- Total revenue
- $0
- Enterprise value
- $137.4M
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