Molecular Classification
Coagulation protein, Glycoprotein, Cofactor
Other Names
Antihemophilic factor, AHF, HEMA
Disease Roles
Coagulation Factor VIII Overview
Coagulation factor VIII (FVIII) is an essential blood clotting protein acting as a cofactor for activated factor IX (FIXa) in the activation of factor X. Deficiency or mutations in FVIII cause hemophilia A, a bleeding disorder. FVIII circulates bound to von Willebrand factor (vWF) and is activated by thrombin. Therapeutic innovations include recombinant FVIII products, gene therapy, and bispecific antibodies.
Mechanism of Action
Cofactor for FIXa-mediated activation of FX in the coagulation cascade, leading to thrombin generation and fibrin clot formation
Biological Functions
Blood coagulation
Hemostasis
Activation of Factor X
Disease Associations
Hemophilia A
von Willebrand disease
Safety Considerations
- Inhibitor development (antibodies against FVIII)
- Thrombosis risk with excessive FVIII replacement
- Immune reactions to FVIII products
Interacting Drugs
Recombinant FVIII
Plasma-derived FVIII
Bispecific antibodies mimicking FVIII
Associated Biomarkers
Biomarker |
---|
FVIII plasma levels |
FVIII activity |