sodium phenylbutyrate
Commercial- Indications
- Urea cycle disorders
Company intelligence / Profile preview
Acer Therapeutics has achieved FDA approval and commercial launch of OLPRUVA™ for certain UCDs. Its pivotal Phase 3 trial of EDSIVO™ in COL3A1-positive vEDS patients remains ongoing. Development of ACER-801 was paused after a Phase 2a trial in VMS and other indications. The company focuses on rare diseases with significant unmet needs.
3 more assets in the full pipeline.
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