Company intelligence / Profile preview

Amylon Therapeutics

Ownership: Private
Employees: ~3
Development stage: Other

Overview

Amylon Therapeutics develops RNA-based therapies targeting rare genetic central nervous system disorders. Its lead program focuses on HCHWA-D/Katwijk’s disease using ASO technology to modulate APP mRNA splicing. The company has several additional preclinical programs targeting neurodegenerative diseases and spinal muscular atrophy. No clinical results have been published yet.

Therapeutic areas: Neurology
Modalities: Antisense oligonucleotides (ASOs)RNA-based therapeuticsBiological products
Industry: Biotech

Drug pipeline

1 asset

APH-1104

Preclinical

Partnerships

ProQR Therapeutics NV—licensing agreement and majority shareholder.

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