Company intelligence / Profile preview
Astellas Gene Therapies
San Francisco, California, United Statesastellasgenetherapies.com ↗
- Ownership
- Private
- Development stage
- Phase 1
01
Overview
Lead program resamirigene bilparvovec (AT132) has advanced into clinical trials targeting X-linked Myotubular Myopathy. AT845 targets Pompe disease and has also entered the clinic. The company continues to expand its pipeline with additional investigational therapies using advanced viral vector platforms but has not yet reached commercial stage with these assets.[10]
- Therapeutic areas
- Rare DiseasesNeurology
- Modalities
- Gene replacement therapy[3][4]Exon skipping gene therapy[3]Vectorized RNA knockdown[3][4]Adeno-associated virus (AAV)-delivered therapies[4][5]
- Industry
- Biotech
02
Drug pipeline
11 assets10 more assets in the full pipeline.
Request access →03
Partnerships
Dyno Therapeutics – collaboration on next-generation AAV vectors using CapsidMap™ technology for skeletal/cardiac muscle applications[6].
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