Company intelligence / Profile preview
Azafaros
- Ownership
- Private
- Employees
- ~23
- Development stage
- Phase 3
Overview
Azafaros has completed both Phase I and II studies with its lead candidate nizubaglustat, an oral small molecule targeting neurological lysosomal storage disorders. The company has also run a multinational natural history study to support future clinical development. Regulatory clearance for global Phase III studies was granted by European authorities in early 2025, with trial initiation planned the same year.
- Therapeutic areas
- Rare Diseases
- Modalities
- Small molecules (specifically, orally available azasugars)
- Industry
- Biotech
Drug pipeline
1 assetPartnerships
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