BBP-671
Phase 1- Indications
- Pantothenate kinase-associated neurodegeneration (PKAN), Propionic acidemia, Methylmalonic acidemia
Company intelligence / Profile preview
The lead compound targets PKAN by increasing activity across the PANK enzyme family to restore or boost cellular coenzyme A synthesis. The company’s approach has advanced into early clinical development with a focus on rare genetic disorders involving impaired energy metabolism. No published pivotal results yet. Pipeline includes additional programs for organic acidurias and other metabolic diseases.
Beyond the preview
Explore clinical development, deal activity, and the competitive landscape with Gosset’s full data platform.
Follow clinical development from trial design and recruitment through results.
Explore licensing agreements, acquisitions, and the assets behind each deal.
Trace financing activity and the investors behind a company’s development.
Compare peer pipelines by target, modality, and therapeutic area.
Explore technology platforms and the patent landscape around relevant assets.
Connect company news and source material to the questions you’re investigating.
See how Gosset can support your research on CoA Therapeutics.