Company intelligence / Profile preview
Epitor Therapeutics
New York, New York, United Statesepitortx.com ↗
- Ownership
- Private
- Employees
- ~4
- Development stage
- Preclinical
01
Overview
Epitor Therapeutics has demonstrated over a 20-fold improvement in targeting efficiency of its CasNano platform and is optimizing this technology for targeted reactivation of silenced genes. The company’s lead program aims to treat Rett syndrome by reactivating the wild-type MeCP2 gene on the inactive X chromosome using an AAV-delivered dCasNano-TETmini editor. Preclinical studies are ongoing, including validation in patient-derived neurons and mouse models.
- Therapeutic areas
- Neurology
- Modalities
- CRISPR-based therapyGene therapyAdeno-associated virus (AAV) deliveryProtein (engineered Cas protein)DNA demethylase fusion protein (TET)
- Industry
- Biotech
02
Drug pipeline
1 asset03
Partnerships
No major pharmaceutical partnerships publicly disclosed as of June 2025.
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