Company intelligence / Profile preview
ExoRNA Bioscience
- Ownership
- Private
- Employees
- ~50
- Development stage
- Other
Overview
The company’s lead asset, ER‑2001, is in Phase 1 trials for Huntington Disease to evaluate safety, tolerability, pharmacokinetics/dynamics, and early efficacy signals using an intravenous exosome-based siRNA approach targeting LAMP‑2. No published efficacy results yet; trial ongoing/recruiting as of April 2025
- Therapeutic areas
- Neurology
- Modalities
- siRNA (small interfering RNA)Nucleic acid drugs delivered via exosome platform
- Industry
- Biotech
Drug pipeline
1 assetBeyond the preview
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