Fondation EspeRare

EspeRare is a non-profit biotech foundation dedicated to revitalizing the development of treatments for rare diseases, particularly those affecting children. By uncovering the potential of existing clinical-stage assets, the foundation accelerates the delivery of life-changing therapies to patients with high unmet medical needs. EspeRare operates through a collaborative model, partnering with pharmaceutical companies, academic institutions, and patient organizations to bridge the gap between laboratory research and commercial availability. Their lead programs include a pioneering in-utero protein replacement therapy for X-linked Hypohidrotic Ectodermal Dysplasia and a small molecule for Duchenne Muscular Dystrophy.