Company intelligence / Profile preview

GeneToBe

Ann Arbor, Michigan, United States
Ownership
Private
Development stage
Other
01

Overview

GeneToBe is developing next-generation genetic therapies using siRNA-based gene silencing and the proprietary MiCas9 CRISPR/Cas9 platform, with programs targeting Cystic Fibrosis, Usher Syndrome, and MASH. The company utilizes genetically-modified rabbit models for preclinical testing, but no clinical results have been reported as of 2025.

Therapeutic areas
PulmonologyMetabolic DisordersRare Diseases
Modalities
Small interfering RNACRISPR-based therapyGene therapy
Industry
Biotech
02

Drug pipeline

4 assets

GTB-ALD-siRNA

Preclinical

3 more assets in the full pipeline.

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