Company intelligence / Profile preview
GeneToBe
- Ownership
- Private
- Development stage
- Other
Overview
GeneToBe is developing next-generation genetic therapies using siRNA-based gene silencing and the proprietary MiCas9 CRISPR/Cas9 platform, with programs targeting Cystic Fibrosis, Usher Syndrome, and MASH. The company utilizes genetically-modified rabbit models for preclinical testing, but no clinical results have been reported as of 2025.
- Therapeutic areas
- PulmonologyMetabolic DisordersRare Diseases
- Modalities
- Small interfering RNACRISPR-based therapyGene therapy
- Industry
- Biotech
Drug pipeline
4 assets3 more assets in the full pipeline.
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