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Larimar Therapeutics
- Ownership
- Public · LRMR
- Employees
- ~65
- Development stage
- Phase 2
Overview
Larimar’s lead candidate nomlabofusp (formerly CTI–1601) has shown dose-dependent increases in frataxin levels and was generally well tolerated with no serious adverse events in Phase 2 studies. The FDA has selected the program for its START pilot to accelerate development. An open-label extension study continues enrolling, and a global Phase 3 trial will begin mid–2025. The company aims to submit a BLA by year-end 2025 seeking accelerated approval using skin FXN concentration as a surrogate endpoint.
- Therapeutic areas
- Neurology
- Modalities
- Protein replacement therapy (fusion proteins)Cell penetrating peptide technology
- Industry
- Biotech
Drug pipeline
5 assets4 more assets in the full pipeline.
Request access →Partnerships
Financials
- Market cap
- $402M
- Total revenue
- $0
- Enterprise value
- $250.7M
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