Company intelligence / Profile preview

Lysosomal and Rare Disorders Research and Treatment Center

Fairfax, Virginia, United States

Ownership: Private
Employees: ~26
Development stage: Other

Overview

LDRTC provides clinical care, translational and clinical research, and participates in clinical trials for innovative therapies (including enzyme replacement and infusion therapies) for lysosomal storage diseases and rare genetic disorders. Their published research has been cited in peer-reviewed journals, and they remain an active hub for clinical studies and patient care.

Therapeutic areas: Rare Diseases
Modalities: Enzyme replacement therapySmall moleculeBiologic
Industry: Academic Hospital/University/Research

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Takeda

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