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Nacuity Pharmaceuticals

Ownership: Private
Development stage: Phase 2

Overview

Nacuity Pharmaceuticals has completed Phase 1 safety studies with its lead candidate NPI‑001 in healthy volunteers. Multiple ongoing Phase 1/2 clinical trials are underway for retinitis pigmentosa associated with Usher syndrome, cataract progression delay via intravitreal implant, nephropathic cystinosis treatment via oral dosage form, and an ophthalmic insert for ocular effects of cystinosis. The company has received orphan drug designations and Fast Track status from the FDA for key programs. No serious adverse events have been reported to date in early clinical studies.

Therapeutic areas: OphthalmologyNeurologyNephrology
Modalities: Small molecules (notably N-acetylcysteine amide [NACA] and analogs)
Industry: Biotech

Drug pipeline

4 assets

N-acetylcysteine amide

3 more assets in the full pipeline.

Partnerships

Foundation Fighting Blindness & RD Fund are major backers/investorsacademic collaborations not explicitly listed but implied by rare disease focus and grant support.

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