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Neela Therapeutics

Lunenburg, Massachusetts, USA
Ownership
Private
Development stage
Other
01

Overview

Neela Therapeutics is a clinical-stage biotechnology company dedicated to advancing precision therapies for rare pediatric neuro-genetic diseases. Established in 2025 as a spin-out from Alcyone Therapeutics following Biogen's acquisition of Alcyone, the company focuses on delivering transformative treatments for complex central nervous system conditions. Neela's lead program, CLN-301, is an AAV9-based gene therapy currently in Phase 1/2 clinical trials for CLN3 Batten disease. The company leverages proprietary platforms including Falcon for precision CNS drug delivery, miREX for X-chromosome reactivation, and Efralex for targeting neurodegenerative pathways.

Therapeutic areas
NeurologyRare Diseases
Modalities
Gene therapySmall moleculeAAV9Precision drug delivery
Industry
Biotech
02

Drug pipeline

2 assets

Efralex

Preclinical

1 more asset in the full pipeline.

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03

Partnerships

Nationwide Children's Hospital

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