Company intelligence / Profile preview

Orphazyme

Ownership: Public · ORPH
Employees: ~17
Development stage: Other

Overview

Orphazyme was a Danish biopharmaceutical company developing small molecule therapies targeting heat shock protein pathways for rare neurodegenerative and lysosomal storage diseases. Its lead candidate arimoclomol advanced through late-stage clinical trials and reached NDA submission for Niemann-Pick disease type C but failed to secure regulatory approval. The company subsequently underwent restructuring and changed its name to Strategic Partners A/S.

Therapeutic areas: Rare DiseasesMetabolic DisordersNeurology
Modalities: Small moleculeProtein therapy
Industry: Biotech

Partnerships

Collaborations with academic institutions in Europe and the United States

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