PTR-01
Phase 1/2- Indications
- Recessive dystrophic epidermolysis bullosa, Dystrophic epidermolysis bullosa
Company intelligence / Profile preview
PTR-01, an intravenously administered recombinant collagen VII protein replacement therapy for RDEB, demonstrated positive results in a Phase 2 trial. The treatment was well-tolerated over four months and led to rapid and durable wound healing with decreased pain reported by all patients who completed the study. No treatment-related serious adverse events were observed in early cohorts
Beyond the preview
Explore clinical development, deal activity, and the competitive landscape with Gosset’s full data platform.
Follow clinical development from trial design and recruitment through results.
Explore licensing agreements, acquisitions, and the assets behind each deal.
Trace financing activity and the investors behind a company’s development.
Compare peer pipelines by target, modality, and therapeutic area.
Explore technology platforms and the patent landscape around relevant assets.
Connect company news and source material to the questions you’re investigating.
See how Gosset can support your research on Phoenix Tissue Repair.