Company intelligence / Profile preview

Reforgene Medicine

Guangzhou, Guangdong, Chinareforgene.com ↗
Ownership
Private
Employees
~3
Development stage
Other
01

Overview

Reforgene Medicine’s lead candidate, RM 001, a genetically modified autologous cell-based gene-editing therapy for beta-thalassaemia, has demonstrated a 100% cure rate in Phase I clinical trials. Pooled efficacy and safety data from phase 0 and phase I/II trials have been presented at major hematology conferences through late 2024. The company is also advancing preclinical programs targeting other genetic diseases.

Therapeutic areas
Rare DiseasesNeurologyOphthalmologyHematologyOncologyOther
Modalities
Gene therapyCell therapyHaematopoietic stem cell therapyGenetically modified autologous cell based therapy
Industry
Biotech
02

Drug pipeline

5 assets

TitanCas12i

Preclinical

4 more assets in the full pipeline.

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