Company intelligence / Profile preview
Rznomics
- Ownership
- Private
- Development stage
- Phase 1
Overview
Rznomics’ lead candidate RZ-001 uses a replication-incompetent adenoviral vector encoding a trans-splicing ribozyme targeting hTERT mRNA. It has reached Phase 1/2a clinical trials for hepatocellular carcinoma and glioblastoma. The company has received Orphan Drug Designation for hepatocellular carcinoma and Fast Track Designation for glioblastoma from the US FDA. Other programs are in IND or preclinical stages targeting genetic eye disorders and neurodegeneration
- Therapeutic areas
- OphthalmologyOncologyNeurology
- Modalities
- RNA-based gene therapytrans-splicing ribozyme technologyAAV-based gene therapy
- Industry
- Biotech
Drug pipeline
6 assets5 more assets in the full pipeline.
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