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Scriptr Therapeutics
Cambridge, Massachusetts, United States
- Ownership
- Private
- Development stage
- Other
01
Overview
Scriptr Therapeutics has demonstrated that StitchR technology can reconstitute high levels of midi-dystrophin protein in muscles and heart of mouse models, with functional improvements in muscle health.[5] The technology enables efficient delivery of larger gene payloads via dual AAV vectors by stitching together gene halves at the RNA level.[5]
- Therapeutic areas
- CardiovascularNeurologyRare Diseases
- Modalities
- Gene therapymRNA-based drugsRNA therapy
- Industry
- Biotech
02
Partnerships
CANbridge Pharmaceuticals (exclusive worldwide research collaboration and licensing agreement for StitchR technology in dystrophinopathies)[3][5]
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