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Spark Therapeutics developed Luxturna (voretigene neparvovec), the first FDA-approved gene therapy for an inherited disease (RPE65-mediated retinal dystrophy). The company has additional gene therapies in development targeting hemophilia A/B and central nervous system diseases. It operates as a subsidiary of Roche since its $4.3–$4.8 billion acquisition in late 2019/early 2020.
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