Company intelligence / Profile preview

SQY Therapeutics

Guyancourt, Île-de-France / Yvelines, Francesqy-therapeutics.com ↗
Ownership
Private
Development stage
Preclinical
01

Overview

SQY Therapeutics has developed a next-generation tricyclo-DNA antisense oligonucleotide platform. Its lead candidate targets exon 51 skipping in the dystrophin gene to treat Duchenne Muscular Dystrophy and is advancing toward or entering Phase 1/2a trials. The company’s tcDNA ASOs show improved RNA binding affinity and tissue distribution compared to earlier generations, with potential applications across multiple genetic diseases. No published clinical results are available yet.

Therapeutic areas
Rare DiseasesNeurology
Modalities
Antisense oligonucleotideTricyclo-DNA class (tcDNA) antisense oligonucleotide
Industry
Biotech
02

Drug pipeline

2 assets

SQY51

2

1 more asset in the full pipeline.

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03

Partnerships

Association Monégasque contre les Myopathies (AMM)Duchenne Parent Project France

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