Company intelligence / Profile preview
SQY Therapeutics
- Ownership
- Private
- Development stage
- Preclinical
Overview
SQY Therapeutics has developed a next-generation tricyclo-DNA antisense oligonucleotide platform. Its lead candidate targets exon 51 skipping in the dystrophin gene to treat Duchenne Muscular Dystrophy and is advancing toward or entering Phase 1/2a trials. The company’s tcDNA ASOs show improved RNA binding affinity and tissue distribution compared to earlier generations, with potential applications across multiple genetic diseases. No published clinical results are available yet.
- Therapeutic areas
- Rare DiseasesNeurology
- Modalities
- Antisense oligonucleotideTricyclo-DNA class (tcDNA) antisense oligonucleotide
- Industry
- Biotech
Drug pipeline
2 assets1 more asset in the full pipeline.
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