Company intelligence / Profile preview

SynaptixBio

Oxford, Oxfordshire, United Kingdomsynaptixbio.com ↗
Ownership
Private
Employees
~1
Development stage
Preclinical
01

Overview

SynaptixBio is developing a treatment for TUBB4A-related leukodystrophy, a rare genetic central nervous system disease. Their therapeutic assets are at a pre-clinical stage of development. The company has secured FDA Orphan Drug Designation and Rare Pediatric Designation for their drug candidate[3][7].

Therapeutic areas
Neurology
Modalities
Antisense oligonucleotides (ASOs)
Industry
Biotech
02

Drug pipeline

3 assets

TUBB4A-shRNA program

Preclinical

2 more assets in the full pipeline.

03

Partnerships

Children's Hospital of Philadelphia (CHOP)

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