Company intelligence / Profile preview
Targeted Genetics Corporation
Seattle, Washington, United Stateslinkedin.com ↗
- Ownership
- Private
- Employees
- ~15
- Development stage
- Preclinical
01
Overview
Targeted Genetics developed AAV-based gene therapies targeting ocular and neurological diseases. Its lead program was an AAV-RPE65 candidate for LCA/severe retinal dystrophies, which reached clinical stage. Other programs included preclinical candidates for Huntington’s disease and ALS. The company struggled financially, sold key manufacturing assets to Genzyme in 2009, and ceased active development shortly thereafter.
- Therapeutic areas
- RheumatologyOphthalmologyNeurologyInfectious Diseases
- Modalities
- Gene therapyRNA interferenceRetroviral vectors
- Industry
- Biotech
02
Drug pipeline
6 assets5 more assets in the full pipeline.
Request access →03
Partnerships
Celladon CorporationAmsterdam Molecular TherapeuticsFred Hutchinson Cancer Research Center
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