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Orchard Therapeutics has developed the approved therapies Libmeldy (atidarsagene autotemcel) for metachromatic leukodystrophy in Europe, UK, Switzerland, and the US, and Strimvelis for adenosine deaminase severe combined immunodeficiency in the EU. The pipeline includes clinical and preclinical-stage gene therapies targeting other rare inherited diseases and neurodegenerative disorders.[2][4][5]
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