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Valerion Therapeutics
Medford, Massachusetts, United Statesmagnify.cnsi.ucla.edu ↗
- Ownership
- Private
- Development stage
- Other
01
Overview
The company developed a proprietary antibody-based system enabling targeted intracellular delivery of proteins, enzymes, and other macromolecules to skeletal muscle tissue. Preclinical data supported proof-of-concept for enzyme replacement in rare neuromuscular diseases but there are no reported clinical results or ongoing trials after rebranding as Valerion Therapeutics. Development appears to have stalled post-preclinical stage by late 2021.
- Therapeutic areas
- Rare DiseasesNeurology
- Modalities
- AntibodyRecombinant proteinEnzyme replacement therapy
- Industry
- Biotech
02
Partnerships
Alopexx Enterprises (management/funding partnership)UCLA (technology licensing)Massachusetts Life Science Center (loan funding)Genzyme Ventures (seed funding)Muscular Dystrophy Association and NIH/HHS grants
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