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ORP-110 is an investigational small molecule developed by OrphoMed, Inc. as a **CFTR (cystic fibrosis transmembrane conductance regulator) stimulant** for the treatment of **cystic fibrosis**. It is designed to enhance CFTR function, potentially addressing the underlying defect in chloride ion transport characteristic of the disease. Currently in the **discovery stage**, with preclinical development focused on this rare genetic disorder affecting the lungs and other organs.[7][19]
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