Clinical trials
Full profile accessFollow clinical development from study design and recruitment through results.
- Trial phase
- Status
- Readouts
Drug intelligence / Profile preview
**SKY-1800** is an investigational small molecule developed by Skyhawk Therapeutics using their proprietary SKYSTAR™ RNA-splicing platform. It functions as a **RNA splicing modulator**, a class of therapies designed to alter pre-mRNA splicing to reduce expression of disease-causing proteins. While specific indications and targets are not publicly detailed, it represents an early-stage candidate akin to Skyhawk's lead asset SKY-0515 for Huntington's disease, potentially targeting RNA-mediated pathologies in rare neurological disorders.[4]
Beyond the preview
Explore the evidence, development activity, and competitive landscape with Gosset’s full data platform.
Follow clinical development from study design and recruitment through results.
Explore development by indication, patient population, and geography.
Trace asset ownership, licensing agreements, and commercial partnerships.
Explore the patent landscape and regulatory exclusivity around an asset.
Compare development programs by target, modality, and indication.
Connect source evidence and development news to your research questions.
See how Gosset can support your research on SKY-1800.