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Myozyme in late-onset Pompe disease
2005-002759-42Phase 3Completed
- Sponsor
- Sanofi
- Start
- Jul 2009
- Modality
- Replacement Enzymes → Therapeutic Enzymes → Recombinant Proteins and Enzymes
- Countries
- 1
01
Overview
Phase 3, randomised, double-blind trial in Pompe disease comparing Myozyme with Placebo (2 arms). Primary endpoints: Safety of Myozyme compared with placebo, Efficacy of Myozyme compared with placebo and 1 more. Started Jul 2009; status: completed.
02
Drugs
alglucosidase alfa
03
Conditions
Pompe disease
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