Trial intelligence / Profile preview

Open-label long-term ganaxolone treatment in infantile spasms

2006-004286-33Phase 2Completed

Sponsor
Marinus Pharmaceuticals
Start
Mar 2007
Modality
Allosteric Modulators → Classical Binding Small Molecules → Small Molecules
Countries
1
01

Overview

Phase 2, open-label, single-arm trial of ganaxolone in West syndrome, sponsored by Marinus Pharmaceuticals. Primary endpoint: Spasm-free status at Week 32. Started Mar 2007; status: completed.

02

Drugs

ganaxolone
03

Conditions

West syndrome

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