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Miglustat for Niemann-Pick disease type C
2006-005842-35Phase 3Active
- Sponsor
- Department of Pediatrics, University of Naples Federico II
- Start
- Oct 2009
- Modality
- Small Molecules
- Countries
- 1
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Overview
Phase 3, single-arm trial of miglustat in Niemann-Pick disease type C (NPC), sponsored by Department of Pediatrics, University of Naples Federico II. Primary endpoints: Neurological involvement progression and Swallowing abnormalities progression. Started Oct 2009; status: active.
02
Drugs
miglustat
03
Conditions
Niemann-Pick disease type C (NPC)
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