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Effects and health economic aspects of enzyme therapy in Pompe disease
2007-001375-11Phase 4Active
- Start
- May 2007
- Modality
- Replacement Enzymes → Therapeutic Enzymes → Recombinant Proteins and Enzymes
- Countries
- 1
01
Overview
Phase 4, open-label, single-arm trial of alglucosidase alfa in Pompe disease. Primary endpoint: Survival. Started May 2007; status: active.
02
Drugs
alglucosidase alfa
03
Conditions
Pompe disease
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