Trial intelligence / Profile preview

Phase III study of GSK2402968 in ambulant Duchenne muscular dystrophy patients amenable to exon 51 skipping

2010-020069-26Phase 3Completed

Sponsor
GSK
Start
Jun 2010
Modality
Small Interfering RNA (siRNA) → Small RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics, MicroRNA (miRNA) → Small RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics, Antisense Oligonucleotides (ASOs) → Long RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics
Countries
1
01

Overview

Phase 3, randomised, double-blind trial in Duchenne muscular dystrophy (DMD) comparing GSK2402968 with Placebo (2 arms). Primary endpoint: Mean change from baseline in 6-minute walk distance. Started Jun 2010; status: completed.

02

Drugs

drisapersen
03

Conditions

Duchenne muscular dystrophy (DMD)

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