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Phase IIa pilot trial of sapropterin on cognitive abilities in young adults with phenylketonuria
2010-024311-13Phase 2Terminated
- Sponsor
- Merck KGaA
- Start
- Jul 2013
- Modality
- Allosteric Modulators → Classical Binding Small Molecules → Small Molecules, Metabolically Activated Prodrugs → Prodrugs/Conditional Activator Small Molecules → Small Molecules
- Countries
- 1
01
Overview
Phase 2, randomised, double-blind trial in phenylketonuria (PKU) comparing Sapropterin with Placebo (2 arms). Started Jul 2013; status: terminated.
02
Drugs
sapropterin
03
Conditions
phenylketonuria (PKU)
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