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Long-term open-label EPI-743 maintenance study in children with Leigh syndrome
2012-001294-84Phase 2Completed
- Sponsor
- Bioelectron
- Start
- Aug 2012
- Modality
- Small Molecules
- Countries
- 1
01
Overview
Phase 2, open-label, single-arm trial of vatiquinone in Leigh syndrome, sponsored by Bioelectron. Primary endpoint: Change in combined Newcastle Pediatric Mitochondrial Disease Scale sections 1-3 score. Started Aug 2012; status: completed.
02
Drugs
vatiquinone
03
Conditions
Leigh syndrome
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