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Long-term extension study of avalglucosidase alfa in Pompe disease
2013-003321-28Phase 2Completed
- Sponsor
- Sanofi
- Start
- Feb 2014
- Modality
- Replacement Enzymes → Therapeutic Enzymes → Recombinant Proteins and Enzymes
- Countries
- 1
01
Overview
Phase 2, open-label, single-arm trial of avalglucosidase alfa in Pompe disease, sponsored by Sanofi. Primary endpoint: Treatment-emergent adverse events and safety. Started Feb 2014; status: completed.
02
Drugs
avalglucosidase alfa
03
Conditions
Pompe disease
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