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COMPASS ataluren study in nonsense mutation mucopolysaccharidosis type I
2014-002596-28Phase 2Completed
- Sponsor
- PTC Therapeutics, Inc.
- Start
- Nov 2014
- Modality
- Small Molecules
- Countries
- 1
01
Overview
Phase 2, single-arm trial of ataluren in mucopolysaccharidosis type I, sponsored by PTC Therapeutics, Inc. Primary endpoint: Overall safety profile of ataluren. Started Nov 2014; status: completed.
02
Drugs
ataluren
03
Conditions
mucopolysaccharidosis type I
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