Study design & results
Available in the Gosset platform where reported.
Trial intelligence / Profile preview
COMPASS ataluren study in nonsense mutation mucopolysaccharidosis type I
2015-003105-41Phase 2Terminated
- Sponsor
- PTC Therapeutics, Inc.
- Start
- Sep 2015
- Modality
- Small Molecules
- Countries
- 1
01
Overview
Phase 2, open-label, single-arm trial of ataluren in mucopolysaccharidosis type I, sponsored by PTC Therapeutics, Inc. Primary endpoint: Overall safety profile of ataluren. Started Sep 2015; status: terminated.
02
Drugs
ataluren
03
Conditions
mucopolysaccharidosis type I
Beyond the preview
Go deeper on 2015-003105-41.
Study design, results and competitive context are available in the Gosset platform where reported.
Competitive context
Available in the Gosset platform where reported.
Bring the full picture into focus.
See how Gosset can support your research on 2015-003105-41.