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Phase 3 retinal gene therapy for choroideremia with AAV2-REP1 (timrepigene emparvovec)

2015-003958-41Phase 3Completed

Sponsor
Nightstar Therapeutics
Start
Mar 2016
Modality
Gene Therapies
Countries
1
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Overview

Phase 3, randomised, single-blind trial of timrepigene emparvovec in choroideremia (2 arms), sponsored by Nightstar Therapeutics. Primary endpoint: Best corrected visual acuity (BCVA) change from baseline. Started Mar 2016; status: completed.

02

Drugs

timrepigene emparvovec
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Conditions

choroideremia

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