Trial intelligence / Profile preview

Long-term safety study of amifampridine phosphate in ambulatory patients with SMA type 3

2018-000160-28Phase 2Terminated

Sponsor
Catalyst Pharmaceuticals
Start
May 2021
Modality
Small Molecules
Countries
1
01

Overview

Phase 2, open-label, single-arm trial of amifampridine in Spinal muscular atrophy type 3 (SMA3), sponsored by Catalyst Pharmaceuticals. Primary endpoint: Long-term safety and tolerability. Started May 2021; status: terminated.

02

Drugs

amifampridine
03

Conditions

Spinal muscular atrophy type 3 (SMA3)

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