Trial intelligence / Profile preview

Efficacy and Safety Study of WVE-210201 in Ambulatory Patients with Duchenne Muscular Dystrophy

2018-004009-22Phase 2

Sponsor
Wave Life Sciences
Start
Mar 2019
Modality
Antisense Oligonucleotides (ASOs) → Long RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics, Single-strand DNA → Antisense DNA → DNA Therapeutics → Nucleic Acid Therapeutics, Modified DNA Oligonucleotides → Antisense DNA → DNA Therapeutics → Nucleic Acid Therapeutics
Countries
1
01

Overview

Phase 2, randomised, double-blind trial in Duchenne muscular dystrophy (DMD) comparing WVE-210201 with Placebo (2 arms). Primary endpoint: Change from baseline in dystrophin level.

02

Drugs

Suvodirsen
03

Conditions

Duchenne muscular dystrophy (DMD)

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