Trial intelligence / Profile preview

Phase 2 Multiple-Ascending-Dose Study of SRP-5051 in Duchenne Muscular Dystrophy

2019-000601-77Phase 2Terminated

Sponsor
Sarepta Therapeutics
Start
Jun 2019
Modality
Peptide-Drug Conjugates → Peptide Conjugates → Peptides, Antisense Oligonucleotides (ASOs) → Long RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics, Single-strand DNA → Antisense DNA → DNA Therapeutics → Nucleic Acid Therapeutics
Countries
1
01

Overview

Phase 2, single-arm trial of Vesleteplirsen in Duchenne muscular dystrophy (DMD), sponsored by Sarepta Therapeutics. Primary endpoint: Primary endpoints Part A. Started Jun 2019; status: terminated.

02

Drugs

Vesleteplirsen
03

Conditions

Duchenne muscular dystrophy (DMD)

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