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Folinic acid in Pearson syndrome and Kearns-Sayre syndrome
2019-003028-19Phase 2Terminated
- Sponsor
- Ospedale Pediatrico Bambino Gesù
- Start
- May 2021
- Modality
- Orthosteric Ligands → Classical Binding Small Molecules → Small Molecules
- Countries
- 1
01
Overview
Phase 2, open-label, single-arm trial of folinic acid in Pearson syndrome and Kearns-Sayre syndrome (KSS), sponsored by Ospedale Pediatrico Bambino Gesù. Primary endpoint: Newcastle Pediatric Mitochondrial Disease Scale Sections 1-3. Started May 2021; status: terminated.
02
Drugs
folinic acid
03
Conditions
Pearson syndromeKearns-Sayre syndrome (KSS)
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