Trial intelligence / Profile preview

Open-Label Extension Study of ISIS 721744 in Patients with Hereditary Angioedema

2020-000197-14Phase 2Active

Sponsor
Ionis Pharmaceuticals
Start
Apr 2020
Modality
Small Interfering RNA (siRNA) → Small RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics, MicroRNA (miRNA) → Small RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics, Antisense Oligonucleotides (ASOs) → Long RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics
Countries
1
01

Overview

Phase 2, open-label, single-arm trial of donidalorsen in hereditary angioedema (HAE), sponsored by Ionis Pharmaceuticals. Primary endpoint: Percentage of participants with at least one treatment-emergent adverse event. Started Apr 2020; status: active.

02

Drugs

donidalorsen
03

Conditions

hereditary angioedema (HAE)

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