Trial intelligence / Profile preview

Effectiveness of ambroxol in children and adults with Gaucher disease type 3: n-of-1 series

2021-002550-82Phase 3Active

Sponsor
Amsterdam University Medical Center
Start
Jul 2022
Modality
Small Molecules
Countries
1
01

Overview

Phase 3, open-label, single-arm trial of ambroxol in Gaucher disease type 3, sponsored by Amsterdam University Medical Center. Started Jul 2022; status: active.

02

Drugs

ambroxol
03

Conditions

Gaucher disease type 3

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