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Phase III crossover study of N-acetyl-L-leucine in Niemann-Pick disease type C
2021-005356-10Phase 3Active
- Sponsor
- IntraBio
- Start
- Dec 2021
- Modality
- Small Molecules
- Countries
- 1
01
Overview
Phase 3, randomised, double-blind trial of levacetylleucine in Niemann-Pick disease type C (NPC) (2 arms), sponsored by IntraBio. Primary endpoint: Scale for the Assessment and Rating of Ataxia. Started Dec 2021; status: active.
02
Drugs
levacetylleucine
03
Conditions
Niemann-Pick disease type C (NPC)
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