Trial intelligence / Profile preview

ENERGY 3 study of INZ-701 in children with ENPP1 deficiency

2023-507382-26-00Phase 3Completed

Sponsor
Inozyme Pharma
Start
May 2024
Modality
Replacement Enzymes → Therapeutic Enzymes → Recombinant Proteins and Enzymes, Fc-Fusion Proteins → Carrier/Scaffold Proteins → Recombinant Proteins and Enzymes
Countries
9
01

Overview

Phase 3, randomised, open-label trial of INZ-701 in ENPP1 deficiency (2 arms), sponsored by Inozyme Pharma. Primary endpoints: Change from baseline in plasma PPi concentration through Week 52 and RGI-C global score through Week 52. Started May 2024; status: completed.

02

Drugs

INZ-701
03

Conditions

ENPP1 deficiency

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