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Open-label extension study of eplontersen (ION-682884) in hereditary transthyretin-mediated amyloid polyneuropathy
2024-511201-32-00Phase 3Authorised
- Sponsor
- Ionis Pharmaceuticals
- Start
- Jun 2022
- Modality
- Antisense Oligonucleotides (ASOs) → Long RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics, Single-strand DNA → Antisense DNA → DNA Therapeutics → Nucleic Acid Therapeutics, Modified DNA Oligonucleotides → Antisense DNA → DNA Therapeutics → Nucleic Acid Therapeutics
- Countries
- 15
01
Overview
Phase 3, open-label, single-arm trial of eplontersen in familial amyloid polyneuropathy (FAP), sponsored by Ionis Pharmaceuticals. Planned start Jun 2022; status: authorised.
02
Drugs
eplontersen
03
Conditions
familial amyloid polyneuropathy (FAP)
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