Trial intelligence / Profile preview

ATLAS-PEDS fitusiran prophylaxis study in children with hemophilia A or B with inhibitors

2024-512501-76-00Phase 3Completed

Sponsor
Sanofi
Start
Jul 2020
Modality
Chemically Modified siRNA → Small Interfering RNA (siRNA) → Small RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics, Conjugated siRNA → Small Interfering RNA (siRNA) → Small RNA Therapeutics → RNA Therapeutics → Nucleic Acid Therapeutics
Countries
6
01

Overview

Phase 3, open-label, single-arm trial of fitusiran in hemophilia A and hemophilia B (HB), sponsored by Sanofi. Primary endpoint: Plasma antithrombin activity levels. Started Jul 2020; status: completed.

02

Drugs

fitusiran
03

Conditions

hemophilia Ahemophilia B (HB)

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